Leukodystrophy Treatments

Treatment

Talk with your doctor about the best treatment plan for you. Treatment options include:

Management of Symptoms

Depending on the type of leukodystrophy and the symptoms, treatment may include:

Medications
Physical, occupational, and/or speech therapy
Nutritional programs
Education
Recreational programs

Bone Marrow Transplant

In a few of the leukodystrophies, bone marrow transplant may help stop the progression of the disease.

Enzyme Replacement Therapy

Replacement of the abnormal or absent enzyme is being explored for a few of the leukodystrophies. Research is being done in this area. Talk to your doctor to find out what treatments may be right for you.

Please be aware that this information is provided to supplement the care provided by your physician. It is neither intended nor implied to be a substitute for professional medical advice. CALL YOUR HEALTHCARE PROVIDER IMMEDIATELY IF YOU THINK YOU MAY HAVE A MEDICAL EMERGENCY. Always seek the advice of your physician or other qualified health provider prior to starting any new treatment or with any questions you may have regarding a medical condition. Copyright © 2026 EBSCO Publishing All rights reserved.