My brothere is 8 years old, he is suffering from duchenne muscular dystrophy, we have been trying to find any cure or treatment since he was 5 years old. We are in desprate need for your help.
I would like to know how can we get him through your exon-skipping therapy trial? Where is your center located? and how FAST can we do that?!?!
Please... Please... we really need your help... and we hope that you might be able to help us in any way!!
Thank you so much! Thank you for your time!